Rodenburg, Lisa W. ; Delpiano, Livia 
; Railean, Violeta ; Centeio, Raquel ; Pinto, Madalena C. ; Smits, Shannon M. A. ; van der Windt, Isabelle S. ; van Hugten, Casper F. J. ; van Beuningen, Sam F. B. ; Rodenburg, Remco N. P. ; van der Ent, Cornelis K. ; Amaral, Margarida D. ; Kunzelmann, Karl ; Gray, Michael A. ; Beekman, Jeffrey M. ; Amatngalim, Gimano D.
; Railean, Violeta ; Centeio, Raquel ; Pinto, Madalena C. ; Smits, Shannon M. A. ; van der Windt, Isabelle S. ; van Hugten, Casper F. J. ; van Beuningen, Sam F. B. ; Rodenburg, Remco N. P. ; van der Ent, Cornelis K. ; Amaral, Margarida D. ; Kunzelmann, Karl ; Gray, Michael A. ; Beekman, Jeffrey M. ; Amatngalim, Gimano D. 
Abstract
Individuals with cystic fibrosis (CF) suffer from severe respiratory disease due to a genetic defect in the cystic fibrosis transmembrane conductance regulator (CFTR) gene, which impairs airway epithelial ion and fluid secretion. New CFTR modulators that restore mutant CFTR function have been recently approved for a large group of people with CF (pwCF), but similar to 19% of pwCF cannot benefit ...
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