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, Rudolph, Günther, Hufendiek, Karsten
, Framme, Carsten, Jägle, Herbert, Salchow, Daniel J., Anschütz, Andreas, Michalakis, Stylianos
and Priglinger, Siegfried G.
(2022)
Gene Therapy with Voretigene Neparvovec Improves Vision and Partially Restores Electrophysiological Function in Pre-School Children with Leber Congenital Amaurosis.
Biomedicines 11 (1), p. 103.
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