Entries of Frangoul, Haydar on the publication server
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Number of items: 2.
Corbacioglu, Selim
, Frangoul, Haydar, Locatelli, Franco, Hobbs, William and Walters, Mark
(2023)
Defining curative endpoints for transfusion‐dependent β‐thalassemia in the era of gene therapy and gene editing.
American Journal of Hematology.
Frangoul, Haydar, Altshuler, David, Cappellini, M. Domenica, Chen, Yi-Shan, Domm, Jennifer, Eustace, Brenda K., Foell, Juergen, de la Fuente, Josu, Grupp, Stephan, Handgretinger, Rupert, Ho, Tony W.
, Kattamis, Antonis, Kernytsky, Andrew, Lekstrom-Himes, Julie, Li, Amanda M., Locatelli, Franco, Mapara, Markus Y., de Montalembert, Mariane, Rondelli, Damiano, Sharma, Akshay
, Sheth, Sujit, Soni, Sandeep, Steinberg, Martin H., Wall, Donna, Yen, Angela and Corbacioglu, Selim
(2021)
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
New England Journal of Medicine 384 (3), pp. 252-260.
Fulltext not available.
, Kattamis, Antonis, Kernytsky, Andrew, Lekstrom-Himes, Julie, Li, Amanda M., Locatelli, Franco, Mapara, Markus Y., de Montalembert, Mariane, Rondelli, Damiano, Sharma, Akshay
, Sheth, Sujit, Soni, Sandeep, Steinberg, Martin H., Wall, Donna, Yen, Angela and Corbacioglu, Selim
(2021)
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
New England Journal of Medicine 384 (3), pp. 252-260.
Fulltext not available.
