Entries of Frangoul, Haydar on the publication server
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Number of items: 2.
2023
Corbacioglu, Selim
, Frangoul, Haydar, Locatelli, Franco, Hobbs, William and Walters, Mark
(2023)
Defining curative endpoints for transfusion‐dependent β‐thalassemia in the era of gene therapy and gene editing.
American Journal of Hematology.
2021
Frangoul, Haydar, Altshuler, David, Cappellini, M. Domenica, Chen, Yi-Shan, Domm, Jennifer, Eustace, Brenda K., Foell, Juergen, de la Fuente, Josu, Grupp, Stephan, Handgretinger, Rupert, Ho, Tony W.
, Kattamis, Antonis, Kernytsky, Andrew, Lekstrom-Himes, Julie, Li, Amanda M., Locatelli, Franco, Mapara, Markus Y., de Montalembert, Mariane, Rondelli, Damiano, Sharma, Akshay
, Sheth, Sujit, Soni, Sandeep, Steinberg, Martin H., Wall, Donna, Yen, Angela and Corbacioglu, Selim
(2021)
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
New England Journal of Medicine 384 (3), pp. 252-260.
Fulltext not available.
, Kattamis, Antonis, Kernytsky, Andrew, Lekstrom-Himes, Julie, Li, Amanda M., Locatelli, Franco, Mapara, Markus Y., de Montalembert, Mariane, Rondelli, Damiano, Sharma, Akshay
, Sheth, Sujit, Soni, Sandeep, Steinberg, Martin H., Wall, Donna, Yen, Angela and Corbacioglu, Selim
(2021)
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
New England Journal of Medicine 384 (3), pp. 252-260.
Fulltext not available.
