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Number of items: 2.

2023

Corbacioglu, Selim , Frangoul, Haydar, Locatelli, Franco, Hobbs, William and Walters, Mark (2023) Defining curative endpoints for transfusion‐dependent β‐thalassemia in the era of gene therapy and gene editing. American Journal of Hematology.

2021

Frangoul, Haydar, Altshuler, David, Cappellini, M. Domenica, Chen, Yi-Shan, Domm, Jennifer, Eustace, Brenda K., Foell, Juergen, de la Fuente, Josu, Grupp, Stephan, Handgretinger, Rupert, Ho, Tony W. , Kattamis, Antonis, Kernytsky, Andrew, Lekstrom-Himes, Julie, Li, Amanda M., Locatelli, Franco, Mapara, Markus Y., de Montalembert, Mariane, Rondelli, Damiano, Sharma, Akshay , Sheth, Sujit, Soni, Sandeep, Steinberg, Martin H., Wall, Donna, Yen, Angela and Corbacioglu, Selim (2021) CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia. New England Journal of Medicine 384 (3), pp. 252-260. Fulltext not available.

This list was generated on Sun Jul 12 06:19:06 2026 CEST.
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